FLT201: Initial Clinical Data

FLT201 demonstrates persistent coverage, while ERT is rapidly eliminated Spleen Bone marrow Lung Untreated Anti-GCase - DAB, Haematoxylin counterstain, AAV8 ERT (1h post-dose) ERT=Velaglucerase alfa ERT (24h post-dose) GBA1 var85 (steady state) FREELNE 14

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