FLT201: Initial Clinical Data

Existing therapies poorly address certain aspects of disease LENGTHY INFUSION EVERY TWO WEEKS PEAKS AND TROUGHS in enzyme levels between infusions allow harmful substrates to build back up of ERT Enzyme replacement therapy current standard of care Easier to reach organs: liver, spleen Harder to reach organs: bone, lung X DOES NOT ADEQUATELY PENETRATE deeper organs, including bone and lung FREELNE7

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